Risdiplam in Type 1 Spinal Muscular Atrophy
Publisher DOI
PubMed ID
33626251
Date Issued
2021
Publication Type
Article
Subject(s)
Language(s)
en
Author(s)
Baranello, Giovanni | |
Darras, Basil T. | |
Day, John W. | |
Deconinck, Nicolas | |
Masson, Riccardo | |
Mercuri, Eugenio | |
Rose, Kristy | |
El-Khairi, Muna | |
Gerber, Marianne | |
Gorni, Ksenija | |
Khwaja, Omar | |
Kletzl, Heidemarie | |
Scalco, Renata S. | |
Seabrook, Timothy | |
Fontoura, Paulo | |
Servais, Laurent |
Journal
New England journal of medicine NEJM
Publisher
Massachusetts Medical Society MMS
ISSN
0028-4793
Access(Rights)
restricted